As of November 2024, approximately 156 clinical trials for Duchenne muscular dystrophy (DMD) are ongoing or pending: 16 trials not yet recruiting, 65 currently recruiting, 28 trials that are active ...
As of November 2024, approximately 137 clinical trials for spinal muscular atrophy (SMA) are ongoing or pending: 8 trials that are not yet recruiting, 74 trials that are currently recruiting, 26 ...
This observational, retrospective study analyzed possible associations between COVID-19 and neuroimmune complications. Patients with COVID-19 who developed chronic inflammatory demyelinating ...
Amorfrutin 2 and magnolol, 2 cannabinoid-like compounds found in noncannabis plants show novel antiseizure activity in mouse models of drug-resistant epilepsy, found a new study published in the ...
Over 31% of patients in the so-called Screening for Cardiac Amyloidosis with Nuclear Imaging in Minority Populations (SCAN-MP) study were women. Transthyretin-mediated amyloid cardiomyopathy (ATTR-CM) ...
Sotatercept at 0.7 mg/kg subcutaneous every 3 weeks optimally balanced efficacy and safety for those with PAH. Sotatercept, a practice-changing therapy for pulmonary arterial hypertension (PAH), ...
This trend corresponds with epidemiological studies performed in Japan and New Zealand, further underscoring a shift in prevalence. The incidence of autoimmune liver diseases (AILDs) such as primary ...
Patients underwent follow-up evaluations on days 4, 10, and 21 post-RS, followed by monthly assessments extending u to 6 months. It is well known that individuals with hemophilia are at an elevated ...
Steve Van Wormer is cofounder and director of the Phaware Global Association, a nonprofit group that raises awareness of pulmonary hypertension (Photo by Larry Luxner) I’m Aware That I’m Rare has had ...
Sandy Siegel, founder and president of the Siegel Rare Neuroimmune Association (Photo by Larry Luxner) Anthropologist Sandy Siegel launched the group after his late wife was diagnosed with transverse ...