Now that I’m in my 30s, navigating life with a progressive muscle disease like limb-girdle muscular dystrophy (LGMD) has been emotionally and mentally challenging. Having Disabled Friends Can Be ...
AlloSCT may offer better prevention of silent cerebral infarcts and improved quality of life in patients with sickle cell disease (SCD). Adjuvant zinc sulfate and ursodeoxycholic acid may reduce ...
Is it Just Pins and Needles? My Journey to a CIDP Diagnosis When my feet started to tingle, I thought it was just pins and needles. When the tingling became numbness and spread up my legs, I started ...
Patients underwent follow-up evaluations on days 4, 10, and 21 post-RS, followed by monthly assessments extending u to 6 months. It is well known that individuals with hemophilia are at an elevated ...
There were no serious adverse events in children who underwent sessions of robot-assisted gait therapy with the device. ATLAS 2030, the medical lower-body exoskeleton for children is safe for patients ...
This case underscores the importance of individualized treatment plans and the need for meticulous perioperative care in patients with bleeding disorders. Among individuals with hemophilia, ...
As of November 2024, approximately 137 clinical trials for spinal muscular atrophy (SMA) are ongoing or pending: 8 trials that are not yet recruiting, 74 trials that are currently recruiting, 26 ...
Avapritinib results in better outcomes among patients with advanced systemic mastocytosis (SM) compared with other therapies, according to new research.
Although nerve parameters examined in AL amyloidosis patients decreased over the last 24 months, they remained in stage I PND. Patients with hereditary transthyretin amyloid polyneuropathy (ATTR-PN) ...
As of November 2024, approximately 156 clinical trials for Duchenne muscular dystrophy (DMD) are ongoing or pending: 16 trials not yet recruiting, 65 currently recruiting, 28 trials that are active ...